New advances offer hope for hemophilia patients

(KYMA, CBS) - Hemophilia is a rare inherited bleeding disorder in which the blood doesn't clot properly, leading to excessive bruising, internal bleeding, and in severe cases, life-threatening complications.

There are two main types: Hemophilia A and the less common Hemophilia B, which affects about one in 20,000 births.

Traditionally, patients required frequent infusions of clotting factor proteins to prevent bleeds. But a newly FDA-approved gene therapy is changing treatment.

By delivering the missing gene directly to the liver, the body can begin producing clotting factor on its own, potentially offering long-term freedom from regular infusions.